346. Targeting the RPGR Gene for Gene Therapy with Highly Specific Nucleases
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چکیده
منابع مشابه
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ژورنال
عنوان ژورنال: Molecular Therapy
سال: 2015
ISSN: 1525-0016
DOI: 10.1016/s1525-0016(16)33955-7